https://pubmed.ncbi.nlm.nih.gov/23590265/
Efficacy and safety of ivacaftor in patients aged 6 to 11 years with cystic fibrosis with a G551D...
In patients who are younger and healthier than those in previously studied populations, ivacaftor demonstrated a significant improvement in pulmonary function,...
https://www.frontiersin.org/journals/pharmacology/articles/10.3389/fphar.2011.00048/full
Frontiers | Stimulation of Wild-Type, F508del- and G551D-CFTR Chloride Channels by Non-Toxic...
Cystic Fibrosis is a major inherited disorder involving abnormalities of fluid and electrolyte transport in a number of different organs due to abnormal func...