https://www.rtihs.org/publications/open-label-phase-2-clinical-trial-mannac-gne-myopathy
Open-label phase 2 clinical trial of ManNAc for GNE myopathy
OBJECTIVE: Assess long-term safety, tolerability, pharmacokinetics, and biochemical effect of ManNAc in subjects with GNE myopathy and identify clinical...
clinical trialopenlabelphase