Robuta

https://pubmed.ncbi.nlm.nih.gov/18157819/ Molecular analysis of SUMF1 mutations: stability and residual activity of mutant... Multiple Sulfatase Deficiency (MSD) is a rare inborn autosomal-recessive disorder, which mainly combines clinical features of metachromatic leukodystrophy,... molecular analysismutationsstabilityresidualactivity