https://www.1nessagency.com/insights/fda-approves-first-gene-therapy-for-pediatric-patients-with
Fayuvi Approval Rewrites Ultra-Rare Disease Marketing as Diagnosis Speed Replaces Patient Volume |...
The FDA approved Fayuvi on September 17, 2026, making it the first treatment for Sanfilippo syndrome type A, a rare pediatric disease that until now had no...
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