https://www.news-medical.net/news/20181121/Genetic-therapy-may-help-children-with-Angelman-syndrome-to-overcome-seizures.aspx
Genetic therapy may help children with Angelman syndrome to overcome seizures
Jun 24, 2019 - Angelman syndrome is a genetic disease with no cure. Children grow up with severe intellectual disabilities and a range of other problems, arguably the worst...
genetic therapymay helpangelman syndromechildren
https://sciencedaily.com/releases/2023/04/230413154253.htm
Genetic therapy corrects progressive muscle disorder in mice | ScienceDaily
Investigators recently used a targeted drug to restore muscle strength and correct myotonia in mice with myotonic dystrophy.
genetic therapyprogressivemuscledisordermice
https://health.ucdavis.edu/crhd/news/headlines/dream-team-to-develop-in-utero-gene-editing-therapy-for-a-rare-neurological-genetic-disorder/2025/09
Dream team to develop in utero gene editing therapy for a rare neurological genetic disorder
Professor Aijun Wang won a $3.2 million NIH grant to develop a cure to Dup15q syndrome using an in-utero gene editing formula.
https://pubmed.ncbi.nlm.nih.gov/20825283/
Genetic engineering of mesenchymal stem cells and its application in human disease therapy
The use of stem cells for tissue regeneration and repair is advancing both at the bench and bedside. Stem cells isolated from bone marrow are currently being...
mesenchymal stem cells
https://www.techtransfer.nih.gov/patent/e-168-1988-1-gb-06
GENE THERAPY USING GENE FUSIONS FOR GENETIC OR ACQUIRED DISORDERS | Technology Transfer
gene therapyusingfusions