https://www.healthday.com/healthpro-news/neurology/fda-approves-miplyffa-for-treatment-of-niemann-pick-disease-type-c
FDA Approves Miplyffa for Treatment of Niemann-Pick Disease, Type C
The U.S. Food and Drug Administration has approved Miplyffa (arimoclomol), an oral medication for the treatment of Niemann-Pick disease, type C.
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https://www.fda.gov/drugs/drug-trials-snapshots/drug-trials-snapshot-miplyffa
Drug Trials Snapshot: MIPLYFFA | FDA
MIPLYFFA is a prescription medicine that is used in combination with miglustat for the treatment of neurological manifestations of Niemann-Pick disease, Type C...
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