https://www.ajmc.com/view/switching-to-gene-therapy-after-nusinersen-or-risdiplam-may-benefit-patients-with-sma
Children with spinal muscular atrophy (SMA) showed motor function improvements after switching to onasemnogene abeparvovec following prior treatment with...
gene therapyswitchingnusinersenrisdiplammay
https://www.ajmc.com/view/repeated-sma-treatment-with-nusinersen-does-not-result-in-consistent-increase-in-immune-responses
The findings, say the researchers, confirm that repeated intrathecal injections of the gene-targeting therapy are safe, adding to the limited data on the...
repeatedsmatreatmentnusinersenresult