Robuta

https://www.pharmaceutical-technology.com/data-insights/propionic-acidemia-drugs-in-development/
GlobalData tracks 5 drugs in development for Propionic Acidemia by five companies/universities/institutes. The top development phase for Propionic Acidemia is...
propionic acidemiadrugsdevelopmentstagestarget
https://www.rivm.nl/publicaties/too-early-to-tell-balancing-diagnostic-accuracy-of-newborn-screening-for-propionic
diagnostic accuracynewborn screeningearlytellbalancing