https://www.ajmc.com/view/switching-to-gene-therapy-after-nusinersen-or-risdiplam-may-benefit-patients-with-sma
Children with spinal muscular atrophy (SMA) showed motor function improvements after switching to onasemnogene abeparvovec following prior treatment with...
gene therapyswitchingnusinersenrisdiplammay
https://mdaquest.org/clinical-research-alert-real-world-study-of-male-fertility-following-risdiplam-treatment/
Nov 19, 2025 - Researchers at Genentech Inc. are seeking adult males treated with risdiplam (Evrysdi) for spinal muscular atrophy (SMA) to participate in an observational...
clinical researchreal worldmale fertilityalertstudy