https://sahmri.org.au/news/events/sahmri-hosts-special-sanfilippo-syndrome-symposium
SAHMRI | SAHMRI hosts special Sanfilippo syndrome symposium
SAHMRI recently partnered with the Sanfilippo Children's Foundation to host a unique symposium.
sanfilippo syndromesahmrihostsspecialsymposium
https://www.progress.org.uk/fda-approves-first-gene-therapy-for-sanfilippo-syndrome-type-a/
FDA approves first gene therapy for Sanfilippo syndrome type A | PET
Sep 28, 2026 - The US FDA has approved the first gene therapy for children with Sanfilippo syndrome type A, a rare condition that causes progressive neurological decline.
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https://www.trialfriend.com/trials/mucopolysaccharidosis-type-iii
Sanfilippo Syndrome (MPS III) Clinical Trial Finder
MPS III clinical trial finder. Search Sanfilippo Syndrome trials recruiting worldwide. Eligibility in plain English and locations near you.
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