https://pompediseasenews.com/news/substrate-reduction-therapy-abx1100-fda-orphan-drug-status/
Substrate Reduction Therapy ABX1100 Granted FDA Orphan Drug Status | Pompe Disease News
Aug 11, 2022 - ABX1100, Aro Biotherapeutics' experimental substrate reduction therapy for Pompe disease, has been granted orphan drug status by the FDA.
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