Robuta

https://pubmed.ncbi.nlm.nih.gov/25988836/
Adeno-associated virus (AAV) is a powerful tool for gene delivery into the brain and has been used for transgene expression in the cerebellar cortex. Although...
transgene expressionpurkinje cellsselectivecerebellargranule
https://pubmed.ncbi.nlm.nih.gov/33718516/
Adeno-associated virus (AAV) vectors are considered efficient vectors for gene transfer, as illustrated by recent successful clinical trials targeting retinal...
long termdeliveryinducesexpressionimmunogenic