https://www.streetwisereports.com/article/2025/10/06/new-drug-for-duchenne-muscular-dystrophy-nears-potential-approval.html
Capricor Therapeutics Inc. (CAPR:NASDAQ) could receive a PDUFA date for its cell therapy as early as spring 2026 if it follows the FDA-outlined path forward,...
duchenne muscular dystrophynew drugpotentialapproval
https://www.justgiving.com/page/jeremy-sharland-1707172908996?utm_source=FB?utm_campaign=009
Help JEREMY Sharland raise money to support Duchenne UK
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https://pubmed.ncbi.nlm.nih.gov/21149430/
By recognizing muscle as a potential source of serum transaminase levels, clinicians can avoid unnecessary and invasive procedures, expedite clinical...
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https://musculardystrophynews.com/assistive-technology-for-duchenne-muscular-dystrophy/
Assistive technology for Duchenne muscular dystrophy includes adaptive aids and modifications that help with independent living.
duchenne muscular dystrophyadaptiveaidsnews
https://www.fiercebiotech.com/biotech/capricor-begin-enrolling-phase-3-dmd-trial-next-quarter-halts-work-mrna-covid-19-vax
Capricor Therapeutics will get enrollment underway in a phase 3 trial for its Duchenne muscular dystrophy (DMD) cell therapy next quarter, while development of...
cullscovidvaxworkeyes
https://whyy.org/segments/hope-devastation-and-finally-a-treatment-one-familys-road-to-gene-therapy-for-duchenne-muscular-dystrophy/
A family in Wilmington, Delaware, faced a looming deadline to get their son a new gene therapy treatment for Duchenne muscular dystrophy.
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https://www.genethon.com/duchenne-muscular-dystrophy-genethon-presents-two-year-consolidated-results-of-the-gnt0004-gene-therapy/
May 19, 2025 - Genethon unveiled the 2-year follow-up data from its GNT0004 gene therapy clinical trial for Duchenne muscular dystrophy, at the American Society of Gene and...
duchenne muscular dystrophypresentstwoyearconsolidated
https://www.streetwisereports.com/article/2025/10/01/biotech-secures-fda-alignment-on-late-stage-duchenne-therapy.html?m_t=2025_10_01_07_27_12
Capricor Therapeutics Inc. (CAPR:NASDAQ) reached agreement with the FDA to include HOPE-3 trial data in its BLA for Deramiocel, its cell therapy for Duchenne...
biotechfdaalignmentlatestage
https://www.afm-telethon.fr/en/news/worldduchenneawarenessday-genethon-Genethon-at-the-forefront-of-the-fight-against-DMD
World Duchenne Muscular Dystrophy Day provides an opportunity to note the acceleration in the development of innovative therapies for this neuromuscular...
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https://www.healthline.com/health/duchenne-muscular-dystrophy-treatment-options?utm_source=ReadNext
Sep 17, 2025 - Treatments such as corticosteroids, physical therapy, and surgery can help manage DMD symptoms and improve quality of life.
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https://www.statnews.com/2025/07/24/duchenne-muscular-dystrophy-families-sarepta-elevydis/
Jul 24, 2025 - A muscular dystrophy disease is devastating on its own, but Sarepta Therapeutics' Elevydis, currently shelved, had offered hope.
sareptafdatangleduchennetherapy
https://www.biopharmadive.com/news/sarepta-duchenne-muscular-dystrophy-ppmo-results/599447/
An experimental Duchenne drug developed with a newer technology may be more potent than Sarepta's marketed treatment Exondys 51. But early data also...
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https://www.chasingconnorscure.co.uk/
Chasing Connor's Cure are on a mission to accelerate funding and research to end duchenne in order to save Connor and boys like him.
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https://www.frontiersin.org/journals/pharmacology/articles/10.3389/fphar.2021.735912/full
Duchenne muscular dystrophy (DMD) is an X-linked condition caused by a deficiency of functional dystrophin protein. Patients experience progressive muscle we...
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https://www.healthline.com/health/duchenne-muscular-dystrophy
Jul 14, 2023 - Learn the symptoms, causes, risks and more of Duchenne muscular dystrophy, a genetic condition causes the muscles to weaken over time.
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https://www.msdmanuals.com/it/casa/problemi-di-salute-dei-bambini/distrofie-muscolari-e-disturbi-correlati/distrofia-muscolare-di-duchenne-e-distrofia-muscolare-di-becker
Distrofia muscolare di Duchenne e distrofia muscolare di Becker - Informazioni su cause, sintomi, diagnosi e trattamento disponibili su Manuali MSD, versione...
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https://www.biopharmadive.com/news/pfizer-duchenne-gene-therapy-phase-3-sarepta/592936/
Sarepta, though, may try to seek accelerated approval using Phase 2 data that's due imminently, along with results from another, smaller trial.
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