https://www.ajmc.com/view/fda-expands-evinacumab-dgnb-approval-for-children-as-young-as-1-year-with-hofh
Evinacumab-dgnb approval expands treatment options for children with homozygous familial hypercholesterolemia (HoFH).
fdaexpandsevinacumabdgnbapproval