Robuta

https://www.frontiersin.org/journals/neurology/articles/10.3389/fneur.2023.1095121/full
ObjectiveNo treatments are approved for Becker muscular dystrophy (BMD). This study investigated the efficacy and safety of givinostat, a histone deacetylase...
becker muscular dystrophyplacebo controlledfrontiersgivinostatrandomized