https://armatusbio.com/
Armatus | Vectorized RNAi for rare neuromuscular disease
Armatus Bio is raising expectations for FSHD with precision gene therapy.
rare neuromusculararmatusvectorizedrnaidisease
https://ern-euro-nmd.eu/registry/
Registry Hub for Rare Neuromuscular Diseases - European Reference Network
rare neuromuscularregistryhubdiseaseseuropean
https://www.rarediseaseadvisor.com/features/tk2d-als-cmt-mda-honors-leaders-rare-disease/
From TK2d to Charcot-Marie-Tooth Disease: MDA Honors Leaders in Rare Neuromuscular Disease
Apr 9, 2026 - Michio Hirano, MD, considered the world’s top expert on TK2d, is the recipient of the MDA’s 2026 Legacy Award for Achievement in Clinical Research.
charcot marie tooth disease