Robuta

https://www.magnitudestudy.com/
Join Intellia Therapeutics in the MAGNITUDE Study, a clinical trial for people living with transthyretin amyloidosis with cardiomyopathy (ATTR-CM).
transthyretin amyloidosisclinical trialmagnitudestudycardiomyopathy
https://www.mdpi.com/2077-0383/13/20/6197
Background: Hereditary transthyretin-related amyloidosis is a clinically heterogeneous autosomal dominant disease caused by pathogenic variants in the TTR gene...
observational studyhereditarytransthyretinrelatedamyloidosis